Vertex executives warned that Casgevy, its curative treatment for sickle cell disease, would be slow to reach patients. But ...

Two Pee Dee siblings are officially cured of sickle cell disease after more than a decade of living with the genetic blood ...

Key HighlightsMotixafortide effectively mobilized sufficient hematopoietic stem cells (HSCs) in patients with sickle cell disease and beta-thalassemia enabling accelerated access to gene therapies73% ...

What you need to know: Gene therapy is a medical treatment that works by changing or fixing a person's genes to treat or prevent disease A biotechnology company in Uganda has developed a new ...

The U.S. Patent and Trademark Office has accepted a groundbreaking patent from Dei BioPharma Ltd., marking a significant milestone in the treatment of sickle cell disease.Dei BioPharma, a Ugandan ...

The nonprofit biotech recently licensed the gene therapy from Boston Children's Hospital and plans to bring it to low- and middle-income countries.

A newly opened sickle cell treatment center at the Medical University of South Carolina is facing growing criticism from ...

A research team has successfully demonstrated the world's first gene-editing treatment for Leber's hereditary optic ...

Parkinson's disease is a progressive neurodegenerative disorder that affects more than one million people in the United States, with approximately 90,000 new cases diagnosed each year. Although ...

A new generation of engineered immune cell destroys cancer cells in mice 1 as effectively as conventional CAR-T-cell ...

The new workflow was adapted from an enzymatic DNA tagging technology, DNA-TAG, previously developed in the Devaraj lab. In ...